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Biomarin Pharmaceuticals(BMRN-Q)
NASDAQ

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Top Stories: Biomarin Pharmaceuticals

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BioMarin-Backed ENERGY 2 Trial Targets High-Value Niche in Ultra-Rare Infant Disease
Analysts Offer Insights on Healthcare Companies: Ascendis Pharma (ASND), BioMarin Pharmaceutical (BMRN) and Ionis Pharmaceuticals (IONS)
BioMarin Halts VOXZOGO Dosing in Select Phase 2 Trials
Wall Street Analysts Are Bullish on Top Healthcare Picks
Cantor Fitzgerald Sticks to Their Buy Rating for BioMarin Pharmaceutical (BMRN)
H.C. Wainwright Remains a Hold on BioMarin Pharmaceutical (BMRN)
Barclays Sticks to Its Buy Rating for BioMarin Pharmaceutical (BMRN)
BioMarin Earnings Call Highlights Growth, Pipeline, Deals
Analysts Offer Insights on Healthcare Companies: Aclaris Therapeutics (ACRS) and BioMarin Pharmaceutical (BMRN)
Evercore ISI Reaffirms Their Buy Rating on BioMarin Pharmaceutical (BMRN)
Cantor Fitzgerald Reaffirms Their Buy Rating on BioMarin Pharmaceutical (BMRN)
Wall Street Analysts Are Bullish on Top Healthcare Picks
Analysts Are Neutral on These Healthcare Stocks: Pliant Therapeutics (PLRX), Summit Therapeutics (SMMT)
BioMarin Pharmaceutical (BMRN) Receives a Buy from Bernstein
Analysts’ Opinions Are Mixed on These Healthcare Stocks: AMN Healthcare Services (AMN), Vanda (VNDA) and BioMarin Pharmaceutical (BMRN)
BioMarin Pharmaceutical (BMRN) Receives a Buy from Canaccord Genuity
BioMarin Raises $850 Million Notes for Amicus Acquisition
BioMarin Pharmaceutical (BMRN) Gets a Buy from Jefferies
BioMarin Secures Major Debt Financing for Amicus Acquisition
BioMarin Announces Major Debt Financing for Amicus Acquisition
BioMarin’s PALace Study: Long-Term Safety Check on Palynziq and What It Means for Investors

Profile

BioMarin Pharmaceutical Inc. focuses on the development and commercialization of treatments for serious life-threatening medical conditions, mostly for children. The company's portfolio comprises seven marketed products namely, Aldurazyme, Naglazyme, Kuvan a rare genetic enzyme deficiency disorder), Vimizim , Brineura, Palynziq and Voxzogo. BioMarin has a collaboration agreement with Sanofi's subsidiary Genzyme for Aldurazyme. Genzyme is BioMarin's sole customer for Aldurazyme and is responsible for marketing and selling Aldurazyme to third parties.'The newest drug in BioMarin's portfolio, Voxzogo for treating achondroplasia, the most common form of dwarfism. BioMarin's biologics license application (BLA) for Roctavian/valoctocogene roxaparvovec (valrox), a gene therapy for severe hemophilia A, was given a complete response letter (CRL) by the FDA.